Targeted manipulation of the sortilin-progranulin axis rescues progranulin haploinsufficiency

Wing C. Lee, Sandra Almeida, Mercedes Prudencio, Thomas R. Caulfield, Yong Jie Zhang, William M. Tay, Peter O. Bauer, Jeannie Chew, Hiroki Sasaguri, Karen R. Jansen-west, Tania F. Gendron, Caroline T. Stetler, Ni Cole Finch, Ian R. Mackenzie, Rosa Rademakers, Fen Biao Gao, Leonard Petrucelli

Research output: Contribution to journalArticlepeer-review

58 Scopus citations

Fingerprint

Dive into the research topics of 'Targeted manipulation of the sortilin-progranulin axis rescues progranulin haploinsufficiency'. Together they form a unique fingerprint.

Medicine & Life Sciences