Genetic Therapy in a Mitochondrial Disease Model Suggests a Critical Role for Liver Dysfunction in Mortality

Ankit Sabharwal, Mark D. Wishman, Roberto Lopez Cervera, Makayla R. Serres, Jennifer L. Anderson, Shannon R. Holmberg, Bibekananda Kar, Anthony J. Treichel, Noriko Ichino, Weibin Liu, Jingchun Yang, Yonghe Ding, Yun Deng, Jean M. Lacey, William J. Laxen, Perry R. Loken, Devin Oglesbee, Steven A. Farber, Karl J. Clark, Xiaolei XuStephen C. Ekker

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