The ISIS-TTRRx-CS2 phase 3 study in patients with familial amyloid polyneuropathy: Baseline results of the first 100 patients for the NIS, NIS+7 and mNIS+7 using different methods of scoring: identification of consistencies and key differences

Rito Bergemann, Elizabeth Ackermann, Brett Monia, Andrew Shenker, P. James B Dyck

Research output: Contribution to journalArticle

Original languageEnglish (US)
Pages (from-to)1-2
Number of pages2
JournalOrphanet Journal of Rare Diseases
Volume10
DOIs
StatePublished - 2015

ASJC Scopus subject areas

  • Medicine(all)
  • Genetics(clinical)
  • Pharmacology (medical)

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