Systematic ranking of inborn errors of metabolism as targets for gene therapy.

Sean E. Hofherr, Dietrich Matern

Research output: Contribution to journalArticlepeer-review

1 Scopus citations
Original languageEnglish (US)
Pages (from-to)215-218
Number of pages4
JournalMolecular genetics and metabolism
Volume100
Issue number3
StatePublished - Jul 2010

ASJC Scopus subject areas

  • Endocrinology, Diabetes and Metabolism
  • Biochemistry
  • Molecular Biology
  • Genetics
  • Endocrinology

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