Prediction of outcome in isolated methylmalonic acidurias: Combined use of clinical and biochemical parameters

Friederike Hörster, S. F. Garbade, T. Zwickler, M. Lindner, S. Kölker, H. I. Aydin, O. A. Bodamer, A. B. Burlina, A. M. Das, J. B.C. De Klerk, C. Dionisi-Vici, S. Geb, G. Gökcay, N. Guffon, E. M. Maier, E. Morava, J. H. Walter, B. Schwahn, F. A. Wijburg, S. GrünewaldM. R. Baumgartner

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