Oral D-galactose supplementation in PGM1-CDG

Sunnie Yan Wai Wong, Therese Gadomski, Monique Van Scherpenzeel, Tomas Honzik, Hana Hansikova, Katja S.Brocke Holmefjord, Marit Mork, Francis Bowling, Jolanta Sykut-Cegielska, Dieter Koch, Jozef Hertecant, Graeme Preston, Jaak Jaeken, Nicole Peeters, Stefanie Perez, David Do Nguyen, Kea Crivelly, Tim Emmerzaal, K. Michael Gibson, Kimiyo RaymondNurulamin Abu Bakar, Francois Foulquier, Gernot Poschet, Amanda M. Ackermann, Miao He, Dirk J. Lefeber, Christian Thiel, Tamas Kozicz, Eva Morava

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Medicine & Life Sciences