Intrathecal/Intracerebroventricular enzyme replacement therapy for the mucopolysaccharidoses: efficacy, safety, and prospects

Roberto Giugliani, Amauri Dalla Corte, Fabiano Poswar, Cláudia Vanzella, Dafne Horovitz, Mariluce Riegel, Guilherme Baldo, Filippo Vairo

Research output: Contribution to journalReview articlepeer-review

7 Scopus citations

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