Enzyme replacement therapy with velaglucerase alfa in Gaucher disease: Results from a randomized, double-blind, multinational, Phase 3 study

Derlis E. Gonzalez, Hadhami Ben Turkia, Elena A. Lukina, Isaac Kisinovsky, Marie Françoise Ben Dridi, Deborah Elstein, David Zahrieh, Eric Crombez, Kiran Bhirangi, Norman W. Barton, Ari Zimran

Research output: Contribution to journalArticlepeer-review

45 Scopus citations

Fingerprint

Dive into the research topics of 'Enzyme replacement therapy with velaglucerase alfa in Gaucher disease: Results from a randomized, double-blind, multinational, Phase 3 study'. Together they form a unique fingerprint.

Medicine & Life Sciences