Enzyme replacement therapy results in substantial improvements in early clinical phenotype in a mouse model of globoid cell leukodystrophy

Wing C. Lee, Andrew Courtenay, Frederick J. Troendle, Melody L. Stallings-Mann, Chad A. Dickey, Michael W. DeLucia, Dennis W. Dickson, Christopher B. Eckman

Research output: Contribution to journalArticle

68 Scopus citations
Original languageEnglish (US)
Pages (from-to)1549-1551
Number of pages3
JournalFASEB Journal
Volume19
Issue number11
DOIs
StatePublished - Sep 1 2005

ASJC Scopus subject areas

  • Biotechnology
  • Biochemistry
  • Molecular Biology
  • Genetics

Cite this

Lee, W. C., Courtenay, A., Troendle, F. J., Stallings-Mann, M. L., Dickey, C. A., DeLucia, M. W., Dickson, D. W., & Eckman, C. B. (2005). Enzyme replacement therapy results in substantial improvements in early clinical phenotype in a mouse model of globoid cell leukodystrophy. FASEB Journal, 19(11), 1549-1551. https://doi.org/10.1096/fj.05-3826fje