Efficacy and safety of N-acetyl-l-leucine in Niemann–Pick disease type C

Tatiana Bremova-Ertl, Jens Claassen, Tomas Foltan, Jordi Gascon-Bayarri, Paul Gissen, Andreas Hahn, Anhar Hassan, Anita Hennig, Simon A. Jones, Miriam Kolnikova, Kyriakos Martakis, Jan Raethjen, Uma Ramaswami, Reena Sharma, Susanne A. Schneider

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Medicine & Life Sciences