D-galactose supplementation in individuals with PMM2-CDG: results of a multicenter, open label, prospective pilot clinical trial

Peter Witters, Hans Andersson, Jaak Jaeken, Laura Tseng, Clara D.M. van Karnebeek, Dirk J. Lefeber, David Cassiman, Eva Morava

Research output: Contribution to journalLetterpeer-review

Fingerprint

Dive into the research topics of 'D-galactose supplementation in individuals with PMM2-CDG: results of a multicenter, open label, prospective pilot clinical trial'. Together they form a unique fingerprint.

Medicine & Life Sciences