Commentary: Current Status of Gene Therapy for Spinal Muscular Atrophy

Wilfried Rossoll, Ravindra N. Singh

Research output: Contribution to journalComment/debatepeer-review

Original languageEnglish (US)
Article number916065
JournalFrontiers in Cellular Neuroscience
Volume16
DOIs
StatePublished - May 17 2022

Keywords

  • AAV9
  • AVXS-101
  • gene therapy
  • onasemnogene abeparvovec
  • spinal muscular atrophy (SMA)
  • Survival Motor Neuron (SMN)
  • Zolgensma

ASJC Scopus subject areas

  • Cellular and Molecular Neuroscience

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