A multicenter open-label treatment protocol (HGT-GCB-058) of velaglucerase alfa enzyme replacement therapy in patients with Gaucher disease type 1: Safety and tolerability

Gregory M. Pastores, Barry Rosenbloom, Neal Weinreb, Ozlem Goker-Alpan, Gregory Grabowski, Gabriel M. Cohn, David Zahrieh

Research output: Contribution to journalArticlepeer-review

17 Scopus citations

Fingerprint

Dive into the research topics of 'A multicenter open-label treatment protocol (HGT-GCB-058) of velaglucerase alfa enzyme replacement therapy in patients with Gaucher disease type 1: Safety and tolerability'. Together they form a unique fingerprint.

Medicine & Life Sciences